natural history study

Highlights from 2025 SciFam: Stronger Together

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August 1- 4, 2025 • Philadelphia, PA Team Titin, together with our partners Cure CMD and A Foundation Building Strength for Nemaline Myopathy, proudly hosted the 2025 SciFam Conference – a four-day gathering for the congenital muscular dystrophy, nemaline myopathy, and titinopathy communities. More than 344 attendees – including affected individuals, families, caregivers, clinicians, researchers, … Read more

Advancing Knowledge for Patients with Titin-Related Centronuclear Myopathy through the TREATIN Project

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Dr. Sarkozy and Prof. Baranello’s project update November 2024 [Stuttgart, Pine Brook, November 8, 2024] – ZNM – Zusammen Stark! e.V., in collaboration with Team Titin, is pleased to share the encouraging one-year results of the TREATIN project (Trial REAdiness for tiTIN-related centronuclear myopathies). Led by Dr Anna Sarkozy and Prof Giovanni Baranello from Great … Read more